‘Transformative moment’ for Irish patients as new access to drug given for rare skin condition epidermolysis bullosa

THE first authorised treatment for a painful and incurable skin condition has been made available in Ireland, in what has ...

LEO Pharma Bolsters Rare Skin Disease Focus Through Acquisition of Replay Gene Therapy Platform

Acquisition adds high-payload herpes simplex virus (HSV) gene therapy targeting genetic skin diseases to LEO Pharma’s ...
Fierce Biotech

Leo Pharma pays $50M for Replay and its preclinical skin disease gene therapy

Danish dermatology specialist Leo Pharma is paying $50 million for U.S. gene writing biotech Replay and its preclinical gene ...
Business Insider

Palvella Therapeutics Highlights Continued Progress Across Rare Skin Disease Pipeline with Two Poster Presentations at the 2026 American Academy of Dermatology Annual Meeting

Poster #76954 highlights QTORIN™ rapamycin’s single phase anhydrous gel formulation designed to optimize dermal bioavailability of rapamycin for mTOR-driven skin diseases while overcoming the ...
Earth.com

Rare skin disease pain may be traced to a single protein target

A key skin protein may control immune overreactions, explaining painful rare conditions and pointing to new treatment paths ...